
Charlie is a joyful 8-year-old who brings light to everyone around him — but every day, he faces the challenges of SLC6A1, a rare genetic disorder that causes seizures, autism, anxiety, OCD, ADHD, behavioral difficulties, and cognitive delays.
After years of relentless work, SLC6A1 Connect and a global team of scientists have helped develop a breakthrough gene therapy designed to treat the root cause of SLC6A1. The therapy exists — but we must fund it so more children can access treatment before time runs out.

You Can Change the Future. Your support directly fuels this gene therapy program, accelerates treatment availability, and gives children like Charlie the chance to live fuller, brighter lives. And right now, every donation is doubled thanks to a $750,000 matching gift, multiplying your impact for kids waiting for their
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Our first ever patient has received gene therapy for SLC6A1. Please help us treat 10 more kids.